
Angelman Syndrome Race Heats Up: $175M Backs Roche's Shelved Drug
247 Health News Editorial
·27 July 2026
·3 min read
·healthtechOak Hill Bio has secured $175 million to revive a Roche-shelved drug for Angelman syndrome, entering a competitive field alongside Ultragenyx and Ionis Pharmaceuticals, both running Phase 3 trials. With pivotal data expected imminently, neurologists and clinical geneticists should begin preparing for a potential paradigm shift in managing this rare, currently untreatable neurogenetic disorder.
Originally reported by STAT News
References
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